Essentials of Genetics (9th Edition) - Standalone book
9th Edition
ISBN: 9780134047799
Author: William S. Klug, Michael R. Cummings, Charlotte A. Spencer, Michael A. Palladino
Publisher: PEARSON
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Chapter CHST6, Problem 6RQ
Summary Introduction
To review:
The case of Ashanti DeSilva who was treated for SCID using gene therapy. To know whether the gene delivered has replaced the defective copy of the ADA gene and analyze the reason for choosing white blood cells as the targets for the therapeutic gene.
Introduction:
The first approved human gene therapy trial was on a 4-year-old girl. This girl named Ashanti DeSilva was suffering from SCID. SCID stands for severe combined immunodeficiency, which is a very rare and inheritable disorder.
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Chapter CHST6 Solutions
Essentials of Genetics (9th Edition) - Standalone book
Ch. CHST6 - What is gene therapy?Ch. CHST6 - Prob. 2RQCh. CHST6 - Prob. 3RQCh. CHST6 - Prob. 4RQCh. CHST6 - Explain how viral vectors can be used for gene...Ch. CHST6 - Prob. 6RQCh. CHST6 - Explain an example of successful gene therapy...Ch. CHST6 - Prob. 8RQCh. CHST6 - Prob. 9RQCh. CHST6 - Describe two gene-silencing techniques and explain...
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